Tofacitinib (4) – Xeljanz®

Ulcerative colitis

Characteristics

Start date 01.09.2018 – Marketing authorisation: 31.07.2018
Resolution 21.02.2019
INN Tofacitinib
Brand name Xeljanz®
Pharm. company Pfizer Pharma GmbH
G-BA Procedure ID D-374
ATC code L04AF01 IMMUNOSUPPRESSANTS (L04A)
ICD-10 codes (AIS) K51.0Backwash ileitis, K51.2Ulcerative (chronic) proctitis, K51.3Ulcerative (chronic) rectosigmoiditis, K51.4Inflammatory polyps of colon, K51.5Left hemicolitis, K51.8Other ulcerative colitis, K51.9Ulcerative colitis, unspecified
Alpha-ID codes (AIS) I115712Chronic ulcerative pancolitis, I115938Left-sided colitis, I26042Ulcerative colitis, I5661Chronic ulcerative proctitis, I5664Chronic rectosigmoiditis ulcerosa, I74949Colitis polyposa
DDD 10 mg O
Therapeutic area Digestive system diseases Ulcerative colitis / Pouchitis
Reason for procedure New therapeutic indication
Specialty Bundling

Therapeutic indication of the resolution

Tofacitinib is indicated for the treatment of adult patients with moderately to severely active ulcerative colitis (UC) who have had an inadequate response, lost response, or were intolerant to either conventional therapy or a biologic agent.

Subpopulation Indication Comparator
a) Adult patients with moderate to severe active ulcerative colitis who have had an inadequate response or no longer respond to conventional therapy, or who have an intolerance or contraindication to conventional therapy TNF-α antagonist (adalimumab or infliximab or golimumab)
b) Adult patients with moderate-to-severe active ulcerative colitis who have had an inadequate response, no longer respond, or are intolerant to a biologic, such as a TNF-α antagonist or integrin inhibitor TNF-α antagonist (adalimumab or infliximab or golimumab) or integrin inhibitor (vedolizumab)

Studies and Results

No. of studies
(best subpopulation)
1 (OCTAVE SUSTAIN)
Study design
(best subpopulation)
H2H vs. non-ACT + no ITC
Meta analysis
(best subpopulation)
no
Reason for dividing into subpopulations (G-BA) Previous treatment

a) Adult patients with moderate to severe active ulcerative colitis who have responded inadequately to conventional therapy, no longer respond to it, or in whom there is intolerance or a contraindication.

  • For adult patients with moderate to severe active ulcerative colitis who have responded inadequately to conventional therapy, no longer respond to it, or in whom there is intolerance or a contraindication, the additional benefit is not proven.
  • For this patient group, the pharmaceutical manufacturer has not provided any comparative studies of tofacitinib against the appropriate comparator therapy.
  • On balance, therefore, an additional benefit is not proven.
  • Overall assessment
    • Consequently, there are no suitable data available for assessing the additional benefit of tofacitinib in the treatment of adult patients with moderate to severe active ulcerative colitis who have responded inadequately to conventional therapy, no longer respond to it, or who have an intolerance or contraindication.

b) Adult patients with moderate to severe active ulcerative colitis who have responded inadequately to a biologic, such as a TNF-α antagonist or integrin inhibitor, no longer respond to it, or who are intolerant to such treatment.

  • For adult patients with moderate to severe active ulcerative colitis who have had an inadequate response to a biologic, such as a TNF-α antagonist or integrin inhibitor, have responded inadequately to a biologic such as a TNF-α antagonist or integrin inhibitor, no longer respond to it, or are intolerant to such treatment, the additional benefit is not proven.
  • For this patient group, the pharmaceutical manufacturer has not submitted any comparative studies of tofacitinib against the appropriate comparator therapy.
  • On balance, therefore, additional benefit is not proven.
  • Overall assessment
    • Consequently, there are no suitable data available for the assessment of the additional benefit of tofacitinib in the treatment of adult patients with moderate to severe active ulcerative colitis who have responded inadequately to a biologic, no longer respond to it, or who are intolerant to such treatment.

Courtesy translation only, please refer to the German original.

Associated procedures

Tofacitinib (7) Xeljanz® Pfizer Pharma GmbH Musculoskeletal system diseases Ankylosing spondylitis (AS) 16,800 100% additional benefit not proven
Tofacitinib (6) Xeljanz® Pfizer Pharma GmbH Musculoskeletal system diseases Polyarticular juvenile idiopathic arthritis, RF+ or RF polyarthritis and dilated oligoarthritis, and juvenile psoriatic arthritis, ≥ 2 years 1,450 100% additional benefit not proven
Tofacitinib (5) Xeljanz® Pfizer Pharma GmbH Musculoskeletal system diseases Rheumatoid arthritis (RA), pretreated patients, monotherapy or combination with methotrexate 27,100–93,500 100% additional benefit not proven
Tofacitinib (3) Xeljanz® Pfizer Pharma GmbH Skin diseases Psoriatic arthritis (PA) 25,900 69% Hint for minor additional benefit
Tofacitinib (4) Xeljanz® Pfizer Pharma GmbH Digestive system diseases Ulcerative colitis 5,300–25,000 100% additional benefit not proven
Tofacitinib (2) Xeljanz® Pfizer Pharma GmbH Musculoskeletal system diseases Rheumatoid arthritis (RA) 0
29,490–63,815
100% additional benefit not proven repealed
Tofacitinib (1) Xeljanz® Pfizer Pharma GmbH Musculoskeletal system diseases Rheumatoid arthritis (RA) 0
87,300–184,470
100% additional benefit not proven repealed


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