Selpercatinib (5) – Retsevmo®

Thyroid carcinoma (MTC), RET-mutated, monotherapy, 12 years and older

Characteristics

Start date 01.10.2022 – Marketing authorisation: 02.09.2022
Resolution 16.03.2023 repealed
Limitation date 01.06.2025
INN Selpercatinib
Brand name Retsevmo®
Pharm. company Lilly Deutschland GmbH
G-BA Procedure ID D-874
ATC code L01EX22 Other protein kinase inhibitors (L01EX)
ICD-10 codes (AIS) C73Malignant neoplasm of thyroid gland
Alpha-ID codes (AIS) I20615Medullary thyroid carcinoma
DDD 0.32 g O
Therapeutic area Oncological diseases Thyroid cancer (DTC / MTC)
Reason for procedure New therapeutic indication
Regulatory status Conditional Approval

Therapeutic indication of the resolution

Retsevmo as monotherapy is used for the treatment of adults and adolescents aged 12 years and older with advanced RET-mutated medullary thyroid carcinoma (MTC), first-line therapy.

Subpopulation Indication Comparator
Adults and adolescents 12 years and older with advanced medullary RET receptor tyrosine kinase (rearranged during transfection - RET)-mutated thyroid carcinoma; first-line therapy - Vandetanib or – cabozantinib

Studies and Results

No. of studies
(best subpopulation)
1 (LIBRETTO-00) 0 (Data not accepted)
Study design
(best subpopulation)
Data not accepted (Dossier: Single-arm + ITC (MAIC))

  • Clinical trials
    • The EXAM trial is a double-blind, international, multicentre RCT comparing cabozantinib with placebo.

Adults and adolescents aged 12 years and over with advanced medullary thyroid carcinoma with a RET receptor tyrosine kinase (rearranged during transfection – RET) mutation; first-line treatment

  • The additional benefit is not proven.
  • Overall, the data presented are not sufficient to demonstrate additional benefit compared with the appropriate comparator therapy; therefore, the additional benefit of selpercatinib as monotherapy in adults and adolescents aged 12 years and over with advanced RET-mutated medullary thyroid carcinoma (MTC) is not proven.
  • Overall assessment
    • The results of the single-arm LIBRETTO-001 study submitted on their own are not suitable for assessing the additional benefit of selpercatinib, as they do not allow for a comparison with the appropriate comparator therapy.
    • The indirect comparison presented, comprising individual arms from various studies in the form of an unweighted comparison, is not suitable for drawing conclusions regarding additional benefit, as the studies are not comparable on either the intervention or control sides with regard to the patients included.
    • Overall, the indirect comparisons presented are not suitable for demonstrating additional benefit over the appropriate comparator therapy; consequently, the additional benefit of selpercatinib as monotherapy in adults and adolescents aged 12 years and over with advanced medullary, It is not proven that the RET receptor tyrosine kinase (rearranged during transfection – RET) mutation is present in first-line treatment.

Courtesy translation only, please refer to the German original.

Associated procedures

Selpercatinib (12) Retsevmo® Lilly Deutschland GmbH Oncological diseases Thyroid carcinoma, RET-fusion-positive, refractory to radioactive iodine, ≥ 2 years n.d. active procedure
Selpercatinib (11) Retsevmo® Lilly Deutschland GmbH Oncological diseases Solid tumours, RET-fusion-positive, aged ≥ 2 to < 18 years n.d. active procedure
Selpercatinib (10) Retsevmo® Lilly Deutschland GmbH Oncological diseases RET-mutated medullary thyroid carcinoma (MTC), ≥ 2 years n.d. active procedure
Selpercatinib (9) Retsevmo® Lilly Deutschland GmbH Oncological diseases Non-small cell lung cancer, RET-fusion+, first-line treatment 155–270 100% additional benefit not proven
Selpercatinib (8) Retsevmo® Lilly Deutschland GmbH Oncological diseases Thyroid carcinoma, RET-mutated, monotherapy, from 12 years of age 40–170 100% Indication of major additional benefit
Selpercatinib (7) Retsevmo® Lilly Deutschland GmbH Oncological diseases Solid tumors, RET-Fusion+ 59–159 100% additional benefit not proven
Selpercatinib (6) Retsevmo® Lilly Deutschland GmbH Oncological diseases Thyroid carcinoma, RET fusion+, refractory to radioiodine, first-line or after systemic prior therapy, ≥ 12 years of age 6–36 100% additional benefit not proven
Selpercatinib (5) Retsevmo® Lilly Deutschland GmbH Oncological diseases Thyroid carcinoma (MTC), RET-mutated, monotherapy, 12 years and older 0
40–170
100% additional benefit not proven repealed
Selpercatinib (4) Retsevmo® Lilly Deutschland GmbH Oncological diseases Non-small cell lung cancer (NSCLC), RET fusion+, first-line 0
115–310
100% additional benefit not proven repealed
Selpercatinib (3) Retsevmo® Lilly Deutschland GmbH Oncological diseases Thyroid carcinoma (MTC), RET fusion+, after sorafenib and/or lenvatinib pre-therapy 2–16 100% additional benefit not proven
Selpercatinib (2) Retsevmo® Lilly Deutschland GmbH Oncological diseases Medullary thyroid carcinoma (MTC), RET-mutated, after cabozantinib and/or vandetanib prior therapy, ≥ 12 years 5–80 100% additional benefit not proven
Selpercatinib (1) Retsevmo® Lilly Deutschland GmbH Oncological diseases Non-small cell lung carcinoma (NSCLC), RET fusion+, after platinum-based chemotherapy and/or immunotherapy 55–200 100% additional benefit not proven


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