Damoctocog alfa pegol (1) – Jivi®

Hemophilia A, ≥ 12 years

Characteristics

Start date 01.01.2019 – Marketing authorisation: 22.11.2018
Resolution 20.06.2019
INN Damoctocog alfa pegol
Brand name Jivi®
Pharm. company Bayer Vital GmbH
G-BA Procedure ID D-425
ATC code B02BD39 Blood coagulation factors (B02BD)
ICD-10 codes (AIS) D66Hereditary factor VIII deficiency
Alpha-ID codes (AIS) I27819Hemophilia A
DDD 1 TU P
Therapeutic area Hematopoietic diseases Hemophilia (Hemophilia A /Hemophilia B)
Reason for procedure Initial assessment

Therapeutic indication of the resolution

Treatment and prophylaxis of bleeding in previously treated patients ≥ 12 years of age with haemophilia A (congenital factor VIII deficiency).

Subpopulation Indication Comparator
Patients aged 12 years and older with haemophilia A (congenital Factor VIII deficiency). Recombinant or human plasma-derived blood coagulation factor VIII preparations

Studies and Results

No. of studies
(best subpopulation)
0 (Data not accepted)
Study design
(best subpopulation)
Data not accepted (Dossier: Uncontrolled study)

  • Clinical trials
    • Study 13024 was an open-label, four-arm, partially randomised study comparing on-demand treatment with prophylactic treatment (three different treatment regimens) using damoctocog alfa pegol in previously treated adolescents (aged 12 to < 18 years) and adult male patients (aged ≥ 18 to 65 years) with severe haemophilia A.
    • The single-arm, non-randomised Phase I study 13401 investigated previously treated male patients with severe haemophilia A.

Patients aged 12 years and over with haemophilia A (congenital factor VIII deficiency)

  • For the treatment and prophylaxis of bleeding in patients aged 12 years and over with haemophilia A (congenital factor VIII deficiency), the additional benefit compared with the appropriate comparator therapy is not proven.
  • The pharmaceutical manufacturer has not provided any relevant data for the assessment of the additional benefit of damoctocog alfa pegol.
  • The G-BA considers that, taken as a whole, the results presented are not sufficient to allow the derivation of patient-relevant effects regarding the additional benefit of damoctocog alfa pegol compared with the appropriate comparator therapy.
  • On balance, therefore, no additional benefit is proven.

Courtesy translation only, please refer to the German original.

Associated procedures

Damoctocog alfa pegol (1) Jivi® Bayer Vital GmbH Hematopoietic diseases Hemophilia A, ≥ 12 years 2,840–3,190 100% additional benefit not proven


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