Calcifediol (1) – Rayaldee®

Secondary hyperparathyroidism in chronic renal failure

Characteristics

Start date 01.02.2022 – Marketing authorisation: 18.08.2020
Resolution 21.07.2022
INN Calcifediol
Brand name Rayaldee®
Pharm. company Fresenius Medical Care Nephrologica Deutschland GmbH
G-BA Procedure ID D-767
ATC code H05BX05 Other anti-parathyroid agents (H05BX)
ICD-10 codes (AIS) N25.8Other disorders resulting from impaired renal tubular function
Alpha-ID codes (AIS) I16639Secondary renal hyperparathyroidism
DDD 30 mcg O
Therapeutic area Metabolic diseases Secondary hyperparathyroidism (sHP)
Reason for procedure Initial assessment – New data exclusivity (known INN)
Specialty ACT change

Therapeutic indication of the resolution

Rayaldee is indicated for the treatment of secondary hyperparathyroidism (sHPT) in adults with stage 3 chronic kidney disease (CKD) and vitamin D deficiency or 4 and vitamin D deficiency.

Subpopulation Indication Comparator
Adult secondary hyperparathyroidism (sHPT) patients with chronic kidney disease stage 3 or 4 and vitamin D deficiency Paricalcitol

Studies and Results

No. of studies
(best subpopulation)
2 (CTAP-CL-3001, CTAP-CL-3002)
Study design
(best subpopulation)
H2H vs. non-ACT + no ITC
Meta analysis
(best subpopulation)
no
ACT change 15.02.2020 – vor Dossiereinreichung

  • Clinical trials
    • The CTAP-CL-3001 and CTAP-CL-3002 trials included adult patients with secondary hyperparathyroidism who had stage 3 or 4 chronic kidney disease and were vitamin D-deficient.

Adults with secondary hyperparathyroidism (sHPT) and stage 3 or 4 chronic kidney disease and vitamin D deficiency

  • For adults with secondary hyperparathyroidism (sHPT) who have stage 3 or 4 chronic kidney disease and vitamin D deficiency, additional benefit is not proven with calcifediol compared with the appropriate comparator therapy.
  • For the assessment of the additional benefit of calcifediol in the treatment of adults with secondary hyperparathyroidism (sHPT) with stage 3 or 4 chronic kidney disease and vitamin D deficiency, the pharmaceutical manufacturer did not submit any suitable data for comparison with the appropriate comparator therapy determined by the G-BA.
  • The studies CTAP-CL-3001 and CTAP-CL-3002 are, in line with the pharmaceutical manufacturer’s assessment, not suitable for evaluating the additional benefit of calcifediol compared with the appropriate comparator therapy, as the appropriate comparator therapy was not implemented.
  • Overall assessment
    • On the basis of the studies submitted, no conclusions can be drawn regarding the additional benefit of calcifediol compared with the appropriate comparator therapy. An additional benefit is therefore not proven.

Courtesy translation only, please refer to the German original.

Associated procedures

Calcifediol (1) Rayaldee® Fresenius Medical Care Nephrologica Deutschland GmbH Metabolic diseases Secondary hyperparathyroidism in chronic renal failure 146,700–184,300 100% additional benefit not proven


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