Acoramidis (1) – Beyonttra®

Hereditary transthyretin amyloidosis in adult patients with cardiomyopathy

Characteristics

Start date 01.04.2025 – Marketing authorisation: 10.02.2025
Resolution 18.09.2025
INN Acoramidis
Brand name Beyonttra®
Pharm. company Bayer Vital GmbH
G-BA Procedure ID D-1167
ATC code C01EB25 Other cardiac preparations (C01EB)
Therapeutic area Metabolic diseases
Reason for procedure Initial assessment

Studies and Results

Adults with wild-type or hereditary transthyretin amyloidosis with cardiomyopathy (ATTR-CM)

  • The additional benefit is not proven.
  • No direct comparative study is available to assess the additional benefit of Acoramidis in comparison with the appropriate comparator therapy, Tafamidis.
  • Overall, there are no suitable data available for assessing the additional benefit of Acoramidis compared with the appropriate comparator therapy, Tafamidis.
  • In summary, it is concluded that, for adults with wild-type or hereditary transthyretin amyloidosis with cardiomyopathy (ATTR-CM), the additional benefit of Acoramidis over the appropriate comparator therapy, Tafamidis, is not proven.

Courtesy translation only, please refer to the German original.

Associated procedures

Acoramidis (1) Beyonttra® Bayer Vital GmbH Metabolic diseases Hereditary transthyretin amyloidosis in adult patients with cardiomyopathy 1,760–2,120 100% additional benefit not proven


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