|
|
|
Nirogacestat
|
Ogsiveo®
|
SpringWorks Therapeutics
|
Oncological diseases
|
Desmoid tumour, advanced
|
Active procedure
Orphan
|
|
|
|
Sebetralstat
|
Ekterly®
|
KalVista Pharmaceuticals
|
Other diseases
|
Hereditary angioedema, acute treatment, ≥ 12 years of age
|
Active procedure
|
|
|
|
Tislelizumab (7)
|
Tevimbra®
|
BeiGene Germany GmbH
|
Oncological diseases
|
Recurrent or metastatic nasopharyngeal carcinoma (NPC), first-line, combination with gemcitabine and cisplatin
|
Active procedure
|
|
|
|
Mirdametinib
|
Ezmekly®
|
SpringWorks Therapeutics
|
Oncological diseases
|
Plexiform neurofibromas (PN), neurofibromatosis type 1 (NF1); ≥ 2 years
|
Active procedure
|
|
|
|
Linvoseltamab
|
Lynozyfic®
|
Regeneron GmbH
|
Oncological diseases
|
Multiple myeloma, at least 3 prior therapies, monotherapy
|
Active procedure
|
|
|
|
Concizumab (3)
|
Alhemo®
|
Novo Nordisk GmbH
|
Hematopoietic diseases
|
Haemophilia A, ≥ 12 years, without factor VIII inhibitors
|
Active procedure
|
|
|
|
Ixekizumab (7)
|
Taltz®
|
Lilly Deutschland GmbH
|
Skin diseases
|
Juvenile psoriatic arthritis, ≥ 6 years
|
Active procedure
|
|
|
|
Ixekizumab (5)
|
Taltz®
|
Lilly Deutschland GmbH
|
Musculoskeletal system diseases
|
Enthesitis-associated arthritis, ≥ 6 years
|
Active procedure
|
|
|
|
Tislelizumab (9)
|
Tevimbra®
|
BeiGene Germany GmbH
|
Oncological diseases
|
Small cell lung carcinoma, first-line, combination with etoposide and platinum chemotherapy
|
Active procedure
|
|
|
|
Tislelizumab (8)
|
Tevimbra®
|
BeiGene Germany GmbH
|
Oncological diseases
|
Non-small cell lung cancer, high risk of recurrence, neoadjuvant and adjuvant therapy, monotherapy or combination with platinum-based chemotherapy
|
Active procedure
|
|
|
|
Trastuzumab deruxtecan (7, reassessment)
|
Enhertu®
|
Daiichi Sankyo Deutschland GmbH
|
Oncological diseases
|
Adenocarcinoma of the stomach or gastro-oesophageal junction, HER2+, after trastuzumab-based therapy
|
Active procedure
|
|
|
|
Resmetirom
|
Rezdiffra®
|
Madrigal Pharmaceuticals
|
Digestive system diseases
|
Metabolic dysfunction-associated steatohepatitis (MASH), non-cirrhotic
|
Active procedure
|
|
|
|
Concizumab (4)
|
Alhemo®
|
Novo Nordisk GmbH
|
Hematopoietic diseases
|
Haemophilia B, ≥ 12 years, without factor IX inhibitors
|
Active procedure
|
|
|
|
Avacopan (2, reassessment)
|
Tavneos®
|
Fresenius Medical Care Nephrologica Deutschland
|
Musculoskeletal system diseases
|
Granulomatosis with polyangiitis or microscopic polyangiitis, combination with rituximab or cyclophosphamide
|
Active procedure
Orphan (turnover limit)
|
|
|
|
Daratumumab (14)
|
Darzalex®
|
Janssen-Cilag GmbH
|
Oncological diseases
|
Multiple myeloma, stem cell transplantation unsuitable, combination with bortezomib, lenalidomide and dexamethasone
|
Active procedure
Orphan (turnover limit)
|
|
|
|
Daratumumab (13)
|
Darzalex®
|
Janssen-Cilag GmbH
|
Oncological diseases
|
Smouldering multiple myeloma (SMM)
|
Active procedure
Orphan (turnover limit)
|
|
|
|
Beremagen geperpavec
|
Vyjuvek®
|
Krystal Biotech
|
Skin diseases
|
Wound treatment for dystrophic epidermolysis bullosa, all age groups
|
Active procedure
Orphan
|
|
|
|
Darolutamid (3)
|
Nubeqa®
|
Bayer Vital GmbH
|
Oncological diseases
|
Prostate carcinoma, metastasised, hormone-sensitive, combination with androgen deprivation therapy
|
Active procedure
|
|
|
|
Lecanemab
|
Leqembi®
|
Eisai GmbH
|
Nervous system diseases
|
Early Alzheimer's disease
|
Active procedure
|
|
|
|
Bulevirtid (4, reassessment >€30m)
|
Hepcludex®
|
Gilead Sciences GmbH
|
Infectious diseases
|
Hepatitis delta virus (HDV) infection, HDV RNA-positive, ≥ 3 years, ≥ 10 kg bw
|
Active procedure
Orphan (turnover limit)
|
|
|
|
Tisotumab vedotin
|
Tivdak®
|
Genmab Germany GmbH
|
Oncological diseases
|
Cervical carcinoma, pre-treated
|
Active procedure
|
|
|
|
Isatuximab (4)
|
Sarclisa®
|
Sanofi-Aventis Deutschland GmbH
|
Oncological diseases
|
Multiple myeloma, first-line, stem cell transplantation suitable, combination with bortezomib, lenalidomide and dexamethasone
|
Active procedure
|
|
|
|
Inavolisib
|
Itovebi®
|
Roche Pharma AG
|
Oncological diseases
|
Breast cancer, PIK3CA-mutated, ER+, HER2-, locally advanced or metastatic, recurrence < 12 months after adjuvant endocrine therapy, combination with palbociclib and fulvestrant
|
Active procedure
|
|
|
|
Deutivacaftor / Tezacaftor / Vanzacaftor
|
Alyftrek®
|
Vertex Pharmaceuticals (Germany) GmbH
|
Metabolic diseases
|
Cystic fibrosis, at least one non-class I mutation, ≥ 6 years of age
|
Active procedure
Orphan
|
|
|
|
Durvalumab (11)
|
Imfinzi®
|
AstraZeneca GmbH
|
Oncological diseases
|
Small cell lung cancer, non-advanced stage, after platinum-based radiochemotherapy, monotherapy
|
Active procedure
|
|
|
|
Durvalumab (10)
|
Imfinzi®
|
AstraZeneca GmbH
|
Oncological diseases
|
Muscle-invasive bladder cancer (MIBC), neoadjuvant/adjuvant therapy after cystectomy, combination with gemcitabine and cisplatin
|
Active procedure
|
|
|
|
Durvalumab (9)
|
Imfinzi®
|
AstraZeneca GmbH
|
Oncological diseases
|
Non-small cell lung cancer, EGFR/ALK-negative, neoadjuvant/adjuvant therapy, combination with platinum-based chemotherapy
|
Active procedure
|
|
|
|
Efgartigimod alfa (3)
|
Vyvgart®
|
Argenx Germany GmbH
|
Nervous system diseases
|
Chronic inflammatory demyelinating polyneuropathy, pre-treated patients
|
Active procedure
Orphan (turnover limit)
|
|
|
|
Odronextamab (2)
|
Ordspono®
|
Regeneron GmbH
|
Oncological diseases
|
Diffuse large B-cell lymphoma (DLBCL), after ≥ 2 prior therapies
|
Active procedure
|
|
|
|
Odronextamab
|
Ordspono®
|
Regeneron GmbH
|
Oncological diseases
|
Follicular lymphoma, after ≥ 2 prior therapies
|
Active procedure
|
|
|
|
Vutrisiran (2)
|
Amvuttra®
|
Alnylam Germany GmbH
|
Metabolic diseases
|
Wild-type or hereditary transthyretin amyloidosis with cardiomyopathy (ATTR-CM)
|
Active procedure
Orphan
|
|
|
|
Givinostat
|
Duvyzat®
|
ITF Pharma GmbH
|
Musculoskeletal system diseases
|
Duchenne muscular dystrophy, ≥ 6 years, combination with a corticosteroid
|
Active procedure
Orphan
|
|
|
|
Remdesivir (5)
|
Veklury®
|
Gilead Sciences GmbH
|
Infectious diseases
|
COVID-19, no need for additional oxygen supply, ≥ 4 weeks, ≥ 3 kg to 40 kg
|
Active procedure
|
|
|
|
Sepiapterin
|
Sephience®
|
PTC Therapeutics International Limited
|
Metabolic diseases
|
Hyperphenylalaninaemia in phenylketonuria
|
Active procedure
Orphan
|
|
|
|
Acalabrutinib (7)
|
Calquence®
|
AstraZeneca GmbH
|
Oncological diseases
|
Chronic lymphocytic leukaemia, first-line, combination with venetoclax
|
Active procedure
|
|
|
|
Acalabrutinib (6)
|
Calquence®
|
AstraZeneca GmbH
|
Oncological diseases
|
Chronic lymphocytic leukaemia, first-line, combination with venetoclax and obinutuzumab
|
Active procedure
|
|
|
|
Acalabrutinib (5)
|
Calquence®
|
AstraZeneca GmbH
|
Oncological diseases
|
Mantle cell lymphoma, no previous BTKi therapy, relapsed or refractory, monotherapy
|
Active procedure
|
|
|
|
Acalabrutinib (4)
|
Calquence®
|
AstraZeneca GmbH
|
Oncological diseases
|
Mantle cell lymphoma, not suitable for ASCT, first-line, combination with bendamustine and rituximab
|
Active procedure
|
|
|
|
Andexanet alfa (2, reassessment)
|
Ondexxya®
|
AstraZeneca GmbH
|
Hematopoietic diseases
|
Repeal of drug anticoagulation
|
Active procedure
|
|
|
|
Nivolumab (32, reassessment)
|
Opdivo®
|
Bristol-Myers Squibb GmbH & Co. KGaA
|
Oncological diseases
|
Carcinoma of the oesophagus or gastro-oesophageal junction, pre-treated patients, adjuvant therapy
|
Active procedure
|
|
|
|
Omaveloxolon (2, reassessment)
|
Skyclarys®
|
Biogen GmbH
|
Nervous system diseases
|
Friedreich's ataxia, ≥ 16 years
|
Active procedure
Orphan (turnover limit)
|
|
|
|
Nivolumab (30)
|
Opdivo®
|
Bristol-Myers Squibb GmbH & Co. KGaA
|
Oncological diseases
|
Non-resectable or advanced hepatocellular carcinoma, first-line, combination with ipilimumab
|
Active procedure
|
|
|
|
Nivolumab (31)
|
Opdivo®
|
Bristol-Myers Squibb GmbH & Co. KGaA
|
Oncological diseases
|
Colorectal cancer with MSI-H or with dMMR, first-line, combination with ipilimumab
|
Active procedure
|
|
|
|
Nivolumab (29)
|
Opdivo®
|
Bristol-Myers Squibb GmbH & Co. KGaA
|
Oncological diseases
|
Non-small cell lung cancer, PD-L1 expression ≥ 1%, neoadjuvant and adjuvant therapy, monotherapy or combination with platinum-based chemotherapy
|
Active procedure
|
|
|
|
Asciminib (2, reassessment >€30m)
|
Scemblix®
|
Novartis Pharma GmbH
|
Oncological diseases
|
Chronic myeloid leukaemia, Ph+, after ≥ 2 prior therapies
|
Active procedure
Orphan (turnover limit)
|
|
|
|
Dalbavancin (3)
|
Xydalba®
|
Advanz Pharma Germany GmbH
|
Infectious diseases
|
Acute bacterial skin and soft tissue infections (ABSSSI), from birth to < 3 months
|
Active procedure
|
|
|
|
Datopotamab deruxtecan
|
Datroway®
|
Daiichi Sankyo Deutschland GmbH
|
Oncological diseases
|
Breast cancer, HR+, HER2-, after at least 1 prior therapy
|
Active procedure
|
|
|
|
Guselkumab (4)
|
Tremfya®
|
Johnson & Johnson
|
Digestive system diseases
|
Ulcerative colitis, pre-treated
|
Active procedure
|
|
|
|
Guselkumab (3)
|
Tremfya®
|
Johnson & Johnson
|
Digestive system diseases
|
Crohn's disease, pre-treated
|
Active procedure
|
|
|
|
Rimegepant (2)
|
Vydura®
|
Pfizer Pharma GmbH
|
Nervous system diseases
|
Migraine acute treatment
|
Active procedure
|
|
|
|
Rimegepant
|
Vydura®
|
Pfizer Pharma GmbH
|
Nervous system diseases
|
Migraine prophylaxis
|
Active procedure
|
|
|
|
Selpercatinib (8, reassessment)
|
Retsevmo®
|
Lilly Deutschland GmbH
|
Oncological diseases
|
Thyroid carcinoma, RET-mutated, monotherapy, from 12 years of age
|
Active procedure
|
|
|
|
Glofitamab (3, reassessment)
|
Columvi®
|
Roche Pharma AG
|
Oncological diseases
|
Diffuse large B-cell lymphoma (DLBCL), after ≥ 2 prior therapies)
|
Active procedure
|
|
|
|
Glofitamab (2)
|
Columvi®
|
Roche Pharma AG
|
Oncological diseases
|
Diffuse large B-cell lymphoma, relapsed or refractory, combination with gemcitabine and oxaliplatin, autologous stem cell transplantation not suitable
|
Active procedure
|
|
|
|
Letermovir (5)
|
Prevymis®
|
MSD Sharp & Dohme GmbH
|
Infectious diseases
|
CMV disease, prophylaxis after kidney transplantation, < 18 years, ≥ 40 kg
|
Active procedure
Orphan (turnover limit)
|
|
|
|
Letermovir (4)
|
Prevymis®
|
MSD Sharp & Dohme GmbH
|
Infectious diseases
|
CMV reactivation/disease, prophylaxis after stem cell transplantation, < 18 years, ≥ 5 kg
|
Active procedure
Orphan (turnover limit)
|
|
|
|
Upadacitinib (8)
|
Rinvoq®
|
AbbVie Deutschland GmbH & Co. KG
|
Musculoskeletal system diseases
|
Giant cell arteritis
|
Active procedure
|